Scientific paper - Original scientific paper
The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products

Palomo, Gloria M.; Pose-Boirazian, Tomas; Naumann-Winter, Frauke; Costa, Enrico; Duarte, Dinah M.; Kalland, Maria E.; Malikova, Eva; Matusevicius, Darius; Vitezić, Dinko; Larsson, Kristina; Magrelli, Armando; Stoyanova-Beninska, Violeta; Mariz, Segundo

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Palomo, G. M., Pose Boirazian, T., Naumann Winter, F., Costa, E., Duarte, D. M., Kalland, M. E. ... Mariz, S. (2023). The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products. Molecular Therapy. doi: 10.1016/j.ymthe.2023.09.020

Palomo, Gloria M., et al. "The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products." Molecular Therapy, 2023. https://doi.org/10.1016/j.ymthe.2023.09.020

Palomo, Gloria M., Tomas Pose Boirazian, Frauke Naumann Winter, Enrico Costa, Dinah M. Duarte, Maria E. Kalland, Eva Malikova, et al. "The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products." Molecular Therapy (2023). https://doi.org/10.1016/j.ymthe.2023.09.020

Palomo, G. M., et al. (2023) 'The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products', Molecular Therapy. doi: 10.1016/j.ymthe.2023.09.020

Palomo GM, Pose Boirazian T, Naumann Winter F, Costa E, Duarte DM, Kalland ME, and sur.. The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products. Molecular Therapy [Internet]. 2023 December [cited 2024 October 01]. doi: 10.1016/j.ymthe.2023.09.020

G. M. Palomo, et al., "The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products", Molecular Therapy, December 2023. [Online]. Available at: https://urn.nsk.hr/urn:nbn:hr:184:382968. [Accessed: 01 October 2024]

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